A daring attempt to use gene therapy to treat a rare, devastating disorder that destroys the brains of children has shown signs of slowing the disease's progression, according to a new paper. However, some experts aren't convinced that the...
WASHINGTON (Reuters) - An experimental gene therapy treatment appears to have helped eight children with a rare and incurable neurological disorder, although it may have been responsible for the death of one, researchers reported on...
TUESDAY, May 13 (HealthDay News) -- A new gene therapy that involves injecting a harmless virus into the brain shows promise as a safe and effective way to slow Batten disease, a rare neurological disorder that usually becomes fatal between the ages...
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Innovative therapy is safe and slows Batten disease progression.
Promising results from a team of NewYork-Presbyterian Hospital/Weill Cornell Medical Center physician-scientists show that gene therapy is both safe and effective at slowing...
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6 months ago from MedicineNet